Rare Diseases Research: Clinical Trial for Niemann-Pick Type C
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Niemann–Pick disease type C Therapeutics Market - NPC Therapeutics Market
Diagnostic workup and management of patients with suspected Niemann-Pick type C disease - Apostolos Papandreou, Paul Gissen, 2016
Miglustat in Niemann-Pick disease type C patients: a review, Orphanet Journal of Rare Diseases
Rare Diseases Research: Clinical Trial for Niemann-Pick Type C
Science Update: Biomarker for Niemann-Pick type C may be useful for diagnosing other class of rare disorders, NIH study suggests
Rare Disease/Orphan Disease
Drug Repurposing for Rare Diseases: Trends in Pharmacological Sciences
Parents of kids with Niemann Pick C advocate for adrabetadex
Niemann-Pick disease type C, Orphanet Journal of Rare Diseases
Case Studies, Clinical Development Case Studies
Niemann–Pick Disease Type C
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por adulto (o preço varia de acordo com o tamanho do grupo)