CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect

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CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Molecular Therapy - Methods & Clinical Development, Gene Editing
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR genome surgery in a novel humanized model for autosomal dominant retinitis pigmentosa: Molecular Therapy
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Correction of the DYSF Gene in Miyoshi Myopathy
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPRi gene modulation and all-optical electrophysiology in post-differentiated human iPSC-cardiomyocytes
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Rapid degeneration of iPSC-derived motor neurons lacking Gdap1 engages a mitochondrial-sustained innate immune response
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
CRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
PDF) CRISPR/Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in Dominant Optic Atrophy patient-derived iPSCs
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Understanding the molecular basis and pathogenesis of hereditary optic neuropathies: towards improved diagnosis and management - ScienceDirect
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Cold shock' increases the frequency of homology directed repair gene editing in induced pluripotent stem cells
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Dead Cas(t) light on new life: CRISPRa-mediated reprogramming of somatic cells into neurons
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Gene augmentation prevents retinal degeneration in a CRISPR/Cas9-based mouse model of PRPF31 retinitis pigmentosa
CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial  homeostasis in dominant optic atrophy patient-derived iPSCs - ScienceDirect
Genome-wide CRISPR/Cas9 deletion screen defines mitochondrial gene essentiality and identifies routes for tumour cell viability in hypoxia
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