Experimental treatment for Niemann-Pick disease appears safe
Por um escritor misterioso
Descrição
An experimental drug has appeared to slow the progression of Niemann-Pick disease the drug 2-hydroxypropyl-beta-cyclodextrin is being tested
Families plead with FDA for drug to treat Niemann-Pick Disease Type C
A Practical Chromogenic Procedure for the Detection of Homozygotes and Heterozygous Carriers of Niemann-Pick Disease
Niemann–Pick type C disease: cellular pathology and pharmacotherapy - Wheeler - 2020 - Journal of Neurochemistry - Wiley Online Library
Ataxia–telangiectasia - Wikipedia
Current advancements in therapy for Niemann-Pick disease: progress and pitfalls: Expert Opinion on Pharmacotherapy: Vol 24, No 11
mRNA Treatment Rescues Niemann–Pick Disease Type C1 in Patient Fibroblasts
Molecular Mind Games: The Medicinal Action of Cyclodextrins in Neurodegenerative Diseases
Therapeutic intervention for Niemann–Pick type C disease must target
NIH teams with industry to develop treatments for Niemann-Pick Type C disease.
Valley boy battling rare disease getting stronger
Valley family fights for drug to save sick child
IJMS, Free Full-Text
New murine Niemann-Pick type C models bearing a pseudoexon-generating mutation recapitulate the main neurobehavioural and molecular features of the disease
de
por adulto (o preço varia de acordo com o tamanho do grupo)
